S13 - Motor Neuron Diseases: Biomarkers, Outcome Measures, and Therapeutics

Event Time: Monday April 24, 2017 1:00 pm to 3:00 pm
Topic(s): Neuromuscular and Clinical Neurophysiology (EMG)
Description: A group of abstracts covering a similar topic presented in an oral format. Presentations are eight minutes in length with four minutes of question and answer. Each session concludes with 25 minutes of a discussant bringing additional context to one or more of the abstracts.
Completion Message:
CME Credits: 2
Core Competencies:

Abstract Presenters

Start Time Pub. Title Presenter
1:00 PM 001 AVXS-101 Phase 1 Gene Therapy Clinical Trial in SMA Type 1: Experience with pre-existing anti-AAV9 antibody in the SMA1 population Douglas M. Sproule, MD
Dr. Sproule has received personal compensation for activities with AveXis, Inc. as an employee. Dr. Sproule holds stock and/or stock options with AveXis, Inc.

1:12 PM 002 AVXS-101 Phase 1 Gene Therapy Clinical Trial in SMA Type 1: Correlation between CHOP-INTEND and Motor Milestone achievements Linda Lowes
Dr. Lowes has nothing to disclose.

1:24 PM 003 A placebo-controlled study to evaluate the safety, tolerability, and preliminary efficacy of BVS857 in patients with spinal and bulbar muscular atrophy Christopher Grunseich, MD
Dr. Grunseich has nothing to disclose.

1:36 PM 004 Reliability of functional outcome measures in spinal muscular atrophy: Results from multi-centered, global, phase 3 clinical trials Allan Glanzman
Dr. Glanzman has nothing to disclose.

1:48 PM 005 Tracking longitudinal evolution of amyotrophic lateral sclerosis using multimodal MRI Pilar Maria Ferraro
Dr. Ferraro has nothing to disclose.

2:00 PM 006 Multimodal structural MRI in the diagnosis of motor neuron diseases Federica Agosta
Dr. Agosta has received personal compensation for consulting, serving on a scientific advisory board, speaking, or other activities with EXCEMED– Excellence in Medical Education.

2:12 PM 007 Patient Activity of Daily Living for Amyotrophic Lateral Sclerosis Laura Herbelin
Dr. Herbelin has nothing to disclose.

2:24 PM 008 Phenotypic heterogeneity in Italian patients with motor neuron disease Nicola Ticozzi, MD
Dr. Ticozzi has nothing to disclose.

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